Search Results

• A Study of Repotrectinib in Pediatric and Young Adult Subjects Harboring ALK, ROS1, OR NTRK1-3 Alterations

  A Phase 1/2, Open-Label, Safety, Tolerability, Pharmacokinetics, and Anti-Tumor Activity Study of Repotrectinib in Pediatric and Young Adult Subjects With Advanced or Metastatic Malignancies Harboring ALK, ROS1, NTRK1-3 Alterations

• Unbalanced Atrioventricular Septal Defect Study

  Unbalanced Atrioventricular Septal Defect: A Congenital Heart Surgeons' Society Inception Cohort Study

• ICN

  Improve Care Now

• International Registry for Severe Chronic Neutropenia

  Severe Chronic Neutropenia International Registry

• Pediatric Precision Laboratory Advanced Neuroblastoma Therapy

  A Study Using Molecular Guided Therapy With Induction Chemotherapy Followed by a Randomized Controlled Trial of Standard Immunotherapy With or Without DFMO Followed by DFMO Maintenance for Subjects With Newly Diagnosed High-Risk Neuroblastoma

• CHSS: Tricuspid Atresia

  Congenital Heart Surgeons’ Society Studies in Congenital Heart Disease: Tricuspid Atresia

• Cystic Fibrosis National Registry

  Cystic Fibrosis National Registry

• NMTT- Neuroblastoma Maintenance Therapy Trial Using DFMO

  NMTT- Neuroblastoma Maintenance Therapy Trial Using Difluoromethylornithine (DFMO)

• Craniopharyngioma - Identifying Bio Targets for Medical Therapy

  Advancing Treatment for Pediatric Craniopharyngioma: Prospective Pilot Study Identifying Clinically Relevant Biological Targets for Medical Therapy

• POWER

  Establishment of the Pediatric Obesity Weight Evaluation Registry (POWER): A prospective pilot project of children and adolescents presenting for weight management.